Coordinated B-globin Expression and A2-Globin Reduction in a Multiplex Lentiviral Gene Therapy Vector for B-thalassemiaTiwaporn Nualkaew,Karine Sii-Felice,Marie Giorgi,Bradley McColl, Julie Gouzil,Astrid Glaser,Hsiao P. J. Voon, Hsin Y. Tee,George Grigoriadis,Saovaros Svasti,Suthat Fucharoen,Suradej Hongeng,Philippe Leboulch,Emmanuel Payen,Jim VadolasMOLECULAR THERAPY(2021)引用 0|浏览0AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要