Correction of F8 Intron 1 Inversion in Hemophilia A Patient-Specific Ipscs by CRISPR/Cas9 Mediated Gene Editing
FRONTIERS IN GENETICS(2023)
关键词
hemophilia A,F8 intron 1 inversion,in situ gene addition,homology-mediated end joining,hepatocyte-like cells
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