Targeting Neuronal Lysosomal Dysfunction Caused by Β-Glucocerebrosidase Deficiency with an Enzyme-Based Brain Shuttle Construct.
Alexandra Gehrlein,Vinod Udayar,Nadia Anastasi,Martino L. Morella,Iris Ruf,Doris Brugger,Sophia von der Mark,Ralf Thoma,Arne Rufer,Dominik Heer,Nina Pfahler,Anton Jochner,Jens Niewoehner,Luise Wolf,Matthias Fueth,Martin Ebeling,Roberto Villaseñor,Yanping Zhu,Matthew C. Deen,Xiaoyang Shan,Zahra Ehsaei,Verdon Taylor,Ellen Sidransky,David J. Vocadlo,Per-Ola Freskgård,Ravi Jagasia NATURE COMMUNICATIONS(2023)
关键词
Lysosomes,Neurodegeneration,Protein delivery,Science,Humanities and Social Sciences,multidisciplinary
AI 理解论文
溯源树
样例
