Collaborative Development of 2-Hydroxypropyl-β-cyclodextrin for the Treatment of Niemann-Pick Type C1 Disease
Elizabeth A. Ottinger,Mark Kao,Nuria Carrillo‐Carrasco,Nicole M. Yanjanin,Roopa Kanakatti Shankar, Marjo J. A. Janssen,Marcus E. Brewster,Ilona Scott,Xin Xu,Jim Cradock,Pramod Terse,Seameen Dehdashti,Juan Marugán,Wei Zheng, Lili Portilla,Alan Hubbs,William J. Pavan,John D. Heiss,Charles H. Vite,Steven U. Walkley,Daniel S. Ory,Steven A. Silber,Forbes D. Porter,Christopher P. Austin,John C. McKew Current topics in medicinal chemistry(2014)
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