Accelerated Endosomal Escape of Splice-Switching Oligonucleotides Enables Efficient Hepatic Splice Correction.
Silvia Weiss,Simon Decker,Christoph Kugler, Laura Bocanegra Gomez, Helene Fasching, Denise Benisch,Fatih Alioglu, Levente Ferencz, Theresa Birkfeld, Filip Ilievski, Volker Baumann, Alina Duran, Enes Dusinovic, Nadine Follrich, Sandra Milenkovic, Dajana Mihalicokova, Daniel Paunov, Karla Singeorzan, Nikolaus Zehetmayer, Dejan Zivanonvic, Ulrich La''chelt,Auke Boersma, Thomas Ruelicke,Haider Sami,Manfred Ogris ACS APPLIED MATERIALS & INTERFACES（2025）
关键词
splice correction,crosslinked polyethylenimine,intravenous,optical tomography,phosphorothioate,endosomal escape,biological barriers
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